Rare Diseases NewsLatest News On Rare Diseases I Spent 40 Years Looking For Answers to My Pain. I Didn’t Know I Had a Rare Genetic Disorder.3/10/2026 5:18 PM FDA to Expedite Approval of Rare Disease Treatments Based on Plausible Mechanisms2/24/2026 10:30 AM Dems Seek To Repeal Orphan-Only Drugs Exemption From Medicare Price Negotiations11/4/2025 3:24 PM Dems Seek Repeal Of Orphan-Only Drugs Exemption From Price Negotiation11/4/2025 2:16 PM How A 60-Year-Old Drug Developer Built A $4.4 Billion Biotech Treating ‘Butterfly Skin Disease’7/31/2025 5:00 AM NIH Launches First Agency-Wide Plan for Autoimmune Disease Research7/25/2025 5:26 AM How EU Price Cuts Are Fuelling a Global Drug Crisis7/16/2025 3:34 AM Sclerosing Mesenteritis: What GIs Need to Know About This Rare Disease6/27/2025 7:31 AM Could Allopurinol Be Marfan’s Lifesaver?6/16/2025 12:37 AM Argentina to Review Use of Fast-track Authorizations for Costly Drugs5/27/2025 9:21 AM
