The Food and Drug Administration (FDA) approved a drug to treat adults with hemophilia B, a rare blood clotting disorder.
“Gene therapy for hemophilia has been on the horizon for more than two decades," said Dr. Peter Marks, director of the FDA’s Center for Biologics Evaluation and Research. “Today’s approval provides a new treatment option for patients with Hemophilia B and represents important progress in the development of innovative therapies for those experiencing a high burden of disease associated with this form of hemophilia.
The FDA reports that about one in 40,000 people has hemophilia B. Most individuals who experience symptoms are men, health officials say.
United States Latest News, United States Headlines
Similar News:You can also read news stories similar to this one that we have collected from other news sources.
FDA Approves First Drug to Delay Onset of Type 1 Diabetes - MedicineNet Health NewsThe U.S. Food and Drug Administration on Thursday approved the first drug that could delay the development of type 1 diabetes (T1D).
Read more »
FDA approves the first-ever drug that can delay the progression of Type 1 diabetesThe drug is an intravenous infusion that can postpone the onset of diabetes in patients.
Read more »
FDA Approves First Drug to Delay Progression of Type 1 DiabetesThe FDA approved the new diabetes treatment Tzield, an injectable treatment that can slow the progression of Type 1 diabetes in patients with stage 2 and delay the need for injectable insulin by two years.
Read more »
FDA approves most expensive drug ever, a $3.5 million-per-dose gene therapy for hemophilia BU.S. health regulators on Tuesday approved the first gene therapy for hemophilia, a $3.5 million one-time treatment for the blood-clotting disorder.
Read more »
Food insecurity jumps this Thanksgiving as food banks struggle with dwindling suppliesOne in five adults reported household food insecurity in 2022, meaning they were unable to acquire adequate food for one or more family members.
Read more »
Perspective | A real-life food critic reviews on-screen food criticsPerspective by Tom Sietsema: How accurately is my profession depicted? To find out, I opened a bottle of wine, fired up YouTube and cable, and reviewed the fictional reviewers.
Read more »