Family raises money for son's gene therapy and clinical trial to treat rare genetic mutation

United States News News

Family raises money for son's gene therapy and clinical trial to treat rare genetic mutation
United States Latest News,United States Headlines
  • 📰 CBSLA
  • ⏱ Reading Time:
  • 22 sec. here
  • 2 min. at publisher
  • 📊 Quality Score:
  • News: 12%
  • Publisher: 51%

Paxton Purdy's parents said he has an ultra-rare neurodegenerative genetic mutation. They hope they can raise enough money to cure it and help children in similar situations.

Paxton Purdy is the sweetest little 7-year-old.'No matter what he's going through, matter what seizures he has, he's the sweetest, most loving boy,' his mom Kristin Purdy said. Paxton's parents said he has an ultra-rare neurodegenerative genetic mutation on his CLCN6 gene. Essentially, it's a chloride channel in his brain that greatly impacts his central nervous system. It caused autism, severe epileptic seizures and affected his ability to walk and talk.

Paul Purdy says Paxton's specific mutation has never been studied meaning the gene therapy is experimental. While the technology is still in its infancy they say a similar gene therapy has proven to be successful. They're reaching out to the community and world to help raise money for Paxton's gene therapy. 'I can't even describe that feeling,' Kristin said. 'It would mean everything to me.

We have summarized this news so that you can read it quickly. If you are interested in the news, you can read the full text here. Read more:

CBSLA /  🏆 552. in US

United States Latest News, United States Headlines

Similar News:You can also read news stories similar to this one that we have collected from other news sources.

‘He’s doing the family proud': Brock Rechsteiner continuing to carry on family name‘He’s doing the family proud': Brock Rechsteiner continuing to carry on family nameBrock Rechsteiner currently has eight receptions for 151 yards and two touchdowns for Jacksonville State.
Read more »

Spy x Family Comes the Closest to Confirming the Desmond Family Secret in One Intense SceneSpy x Family Comes the Closest to Confirming the Desmond Family Secret in One Intense SceneDamian and his parents in Spy x Family chapter 106
Read more »

'SNL' takes aim at Kamala Harris' 'middle class family' response during 'Family Feud' skit'SNL' takes aim at Kamala Harris' 'middle class family' response during 'Family Feud' skitSNL mocked VP Kamala Harris again on Saturday, taking aim at a story about growing up in a middle class family, which the vice president has told several times.
Read more »

Prince William Will Reportedly Snub Royal Family's Christmas if This Family Member Is InvitedPrince William Will Reportedly Snub Royal Family's Christmas if This Family Member Is InvitedAmy Mackelden is a contributing editor at Marie Claire, where she covers celebrity and royal family news. She was the weekend editor at Harper’s BAZAAR for three years, where she covered breaking celebrity and entertainment news, royal stories, fashion, beauty, and politics.
Read more »

Presley Family Puts Drama Behind Them, Prioritizes FamilyPresley Family Puts Drama Behind Them, Prioritizes FamilyThe Presley family, known globally for their music and celebrity status, is focusing on unity after a period of public legal disputes. Following the death of Lisa Marie Presley, her mother Priscilla Presley and granddaughter Riley Keough faced legal challenges regarding the control of Elvis Presley's estate.
Read more »

49ers Studs and Duds: Brock Purdy’s disaster game adds insult to injuries49ers Studs and Duds: Brock Purdy’s disaster game adds insult to injuriesBrock Purdy’s three interceptions were just the tip of an iceberg of bad play for the Niners.
Read more »



Render Time: 2025-02-21 01:50:43